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Study details
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A Study of BTX-A51 in People With Relapsed or Refractory Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

Edgewood Oncology Inc.
NCT IDNCT04243785ClinicalTrials.gov data as of Apr 2026
Phase

Phase 1

Target enrollment

80

Study length

about 7.2 years

Ages

18+

Locations

3 sites in CA, NY, TX

About this study

Researchers are testing a treatment called BTX-A51 to see if it's safe and effective for people with relapsed or refractory acute myeloid leukemia (AML) or high-risk myelodysplastic syndrome (MDS). The trial will involve different doses of BTX-A51, either alone or in combination with azacitidine. Participants may receive treatment for up to eight 28-day cycles if their doctor thinks it's beneficial.

Based on ClinicalTrials.gov records.

What participants do

  • 1.Take Azacitidine
  • 2.Take BTX-A51
PhasePhase 1
DrugAzacitidine
Routeinjection
Primary goalIncidence of dose-limiting toxicities (DLTs)

Participation effort

Estimated from trial records. Details can vary by site.

Time + visits
Low13%
Logistics
Moderate50%

Logistics difficulty varies by site location and availability.

Trial highlights

Treatment details

Auto-extracted from trial records to preview treatments and outcomes.

Drug classes

azacitidine

Drug routes

injection, subcutaneous

Endpoints

Primary: Incidence of dose-limiting toxicities (DLTs), Maximum tolerated dose (MTD), Number of participants with 12-lead electrocardiogram (ECG) abnormalities and/or AEs, Number of participants with echocardiogram (ECHO) abnormalities and/or AEs, Number of participants with laboratory abnormalities and/or AEs, Number of participants with non-serious AEs and serious AEs (SAEs), Number of participants with physical examination abnormalities and/or AEs, Number of participants with vital sign abnormalities and/or AEs

Secondary: Complete remission (CR) for participants with acute myeloid leukemia (AML), Complete remission (CR) for participants with high-risk myelodysplastic syndrome (MDS), Overall survival and event-free survival in participants with AML or high-risk MDS, PK parameter: AUC0-24, PK parameter: AUC0-24D5, PK parameter: C0, PK parameter: Maximum observed plasma concentration (Cmax), PK parameter: Plasma CmaxD5

Body systems

Oncology